«Mavacamten shows broad benefit in human and mouse models of MYBPC3-related hypertrophic cardiomyopathy»

Sen-Martín L, Fernández-Trasancos Á, López-Unzu MÁ, Bak A, Zafra-Castellano M, Srikantharajah R, Pathak D, Klotz A, Kuehn MN, Ferrarini A, Labrador-Cantarero V, Sánchez-Ortiz D, Pricolo MR, Vicente N, Velázquez-Carreras D, Sánchez-García L, Sicilia J, Nicolás-Ávila JÁ, Sánchez-Díaz M, Schlossarek S, Cussó L, Desco M, Villalba-Orero M, Guzmán-Martínez G, Calvo E, Barriales-Villa R, Vázquez J, Sánchez-Cabo F, Hidalgo A, de Tombe PP, Carrier L, Spudich JA, Ruppel KM, Weinberger F, Cazorla O, Hessel AL, Alegre-Cebollada J.

 Nat Cardiovasc Res. 2026 Jul;5(7):638-657. https://doi.org/10.1038/s44161-026-00833-3